MIGALASTAT SWITCHSummary: Evaluation of Biomarkers for patients receiving migalastat after switching from ERT.
MIGALASTAT SWITCH
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sEARCH RESULTS
FABRY HCM
Screening for Fabry cardiomyopathy using cardiac magnetic resonance imaging.
PERIDOT – Patient ExpeRIence in fabry Disease On venglustaT
A randomized, double-blind, placebo-controlled, 12-month Phase III study to evaluate the effect of Venglustat on neuropathic and abdominal pain in male and female adults with Fabry disease who are treatment-naive or untreated for at least 6 months